Gene Therapy, from Hollywood to the bench to the clinic
When: | Tuesday, 11 November 2025 - Tuesday, 11 November 2025 |
Where: | PVT Resource Center, Ground Floor, PVT Building, 29 Princess of Wales Terrace, Parktown. |
Start time: | 15:00 |
Enquiries: | For enquiries please email : idori.research@wits.ac.za |
RSVP: | https://forms.office.com/r/dKTM8bY5wg?origin=lprLink |
Dr Simon Waddington will present a seminar on 11 November 2025 from 15h00 - 16h30.
Inherited genetic diseases are individually rare but, collectively, affect over 400 million people worldwide; over 75% are children. For many young people with these conditions there is little hope. Most rare genetic diseases are untreatable, causing significant disability, with almost a third dying before their fifth birthday. Licensed genetic treatments are currently available for less than 0.1% of patients with these diseases, leading to significant morbidity and premature mortality. In this lecture, He will explore the public perception of gene therapy and detail one of our clinical-trajectory gene therapy programmes.
